GBM Lunch
Annemieke Aartsma-Rus: Development of exon skipping ASO therapy for Duchenne and the lessons we learned along the way
24.09.2025
12:30-13:30
Speaker: Annemieke Aartsma-Rus (Leiden University)
Chair: Julia Weigand (Philipps-Universität Marburg, Institut für Pharmazeutische Chemie)
Organizers: GBM Study Group RNA Biochemistry